Lenmeldy | atidarsagene autotemcel | Orchard Therapeutics | 4.25 |
---|---|---|---|
Beqvez ; Hemgenix | fidanacogene elaparvovec ; etranacogene dezaparvovec | Pfizer; CSL Behring | 3.50 |
Elevidys | delandistrogene moxeparvovec | Sarepta Therapeutics | 3.20 |
Lyfgenia | lovotibeglogene autotemcel | bluebird bio | 3.10 |
Skysona | elivaldogene autotemcel | bluebird bio | 3.00 |
Rethymic | allogeneic processed thymus tissue | Enzyvant | 2.81 |
Zynteglo | autologous cd34+ cells (ba-t87q-globin gene) | bluebird bio | 2.80 |
Zolgensma | onasemnogene abeparvovec | Novartis | 2.32 |
Casgevy | exagamglogene autotemcel | Vertex and CRISPR Therapeutics | 2.20 |