Selection of gene therapies approved by the US Food and Drug Administration since 2019. All are single-dose treatments.
ZOLGENSMA | 2019 | 2,125,000 |
---|---|---|
HEMGENIX | 2022 | 3,500,000 |
ZYNTEGLO | 2022 | 2,800,000 |
SKYSONA | 2022 | 3,000,000 |
ROCTAVIAN | 2023 | 2,900,000 |
ELEVIDYS | 2023 | 3,200,000 |
LYFGENIA | 2023 | 3,100,000 |
CASGEVY | 2023 | 2,200,000 |
LIBMELDY | 2024 | 4,250,000 |